Mini-COMET study: Individual participant-level responses to treatment in patients with infantile-onset Pompe disease receiving repeated dose regimens of avalglucosidase alfa or alglucosidase alfa who were previously treated with alglucosidase alfa
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Kishnani, PS; Brassier, A; Broomfield, A; Davison, J; Hahn, SH; Kumada, S; Labarthe, F; Ohki, H; Pichard, S; Haack, KA; Johnson, J; Meng, X ...
Published in: Molecular Genetics and Metabolism
February 2021
Duke Scholars
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2021
Volume
132
Issue
2
Start / End Page
S57 / S58
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences
Citation
APA
Chicago
ICMJE
MLA
NLM
Kishnani, P. S., Brassier, A., Broomfield, A., Davison, J., Hahn, S. H., Kumada, S., … Kronn, D. (2021). Mini-COMET study: Individual participant-level responses to treatment in patients with infantile-onset Pompe disease receiving repeated dose regimens of avalglucosidase alfa or alglucosidase alfa who were previously treated with alglucosidase alfa. In Molecular Genetics and Metabolism (Vol. 132, pp. S57–S58). Elsevier BV. https://doi.org/10.1016/j.ymgme.2020.12.128
Kishnani, Priya S., Anaïs Brassier, Alexander Broomfield, James Davison, Si Houn Hahn, Satoko Kumada, François Labarthe, et al. “Mini-COMET study: Individual participant-level responses to treatment in patients with infantile-onset Pompe disease receiving repeated dose regimens of avalglucosidase alfa or alglucosidase alfa who were previously treated with alglucosidase alfa.” In Molecular Genetics and Metabolism, 132:S57–58. Elsevier BV, 2021. https://doi.org/10.1016/j.ymgme.2020.12.128.
Kishnani PS, Brassier A, Broomfield A, Davison J, Hahn SH, Kumada S, et al. Mini-COMET study: Individual participant-level responses to treatment in patients with infantile-onset Pompe disease receiving repeated dose regimens of avalglucosidase alfa or alglucosidase alfa who were previously treated with alglucosidase alfa. In: Molecular Genetics and Metabolism. Elsevier BV; 2021. p. S57–8.
Kishnani, Priya S., et al. “Mini-COMET study: Individual participant-level responses to treatment in patients with infantile-onset Pompe disease receiving repeated dose regimens of avalglucosidase alfa or alglucosidase alfa who were previously treated with alglucosidase alfa.” Molecular Genetics and Metabolism, vol. 132, no. 2, Elsevier BV, 2021, pp. S57–58. Crossref, doi:10.1016/j.ymgme.2020.12.128.
Kishnani PS, Brassier A, Broomfield A, Davison J, Hahn SH, Kumada S, Labarthe F, Ohki H, Pichard S, Haack KA, Johnson J, Meng X, Chien Y-H, Kronn D. Mini-COMET study: Individual participant-level responses to treatment in patients with infantile-onset Pompe disease receiving repeated dose regimens of avalglucosidase alfa or alglucosidase alfa who were previously treated with alglucosidase alfa. Molecular Genetics and Metabolism. Elsevier BV; 2021. p. S57–S58.
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2021
Volume
132
Issue
2
Start / End Page
S57 / S58
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences