NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in participants with late-onset pompe disease (LOPD)
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Dimachkie, MM; Barohn, RJ; Byrne, B; Goker-Alpan, O; Kishnani, PS; Ladha, S; Laforêt, P; Mengel, KE; Pena, LDM; Sacconi, S; Straub, V; Lu, X ...
Published in: Molecular Genetics and Metabolism
February 2021
Duke Scholars
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2021
Volume
132
Issue
2
Start / End Page
S34 / S34
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences
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APA
Chicago
ICMJE
MLA
NLM
Dimachkie, M. M., Barohn, R. J., Byrne, B., Goker-Alpan, O., Kishnani, P. S., Ladha, S., … Benedikt Schoser; on behalf of NEO-EXT investigators, . (2021). NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in participants with late-onset pompe disease (LOPD). In Molecular Genetics and Metabolism (Vol. 132, pp. S34–S34). Elsevier BV. https://doi.org/10.1016/j.ymgme.2020.12.064
Dimachkie, Mazen M., Richard J. Barohn, Barry Byrne, Ozlem Goker-Alpan, Priya S. Kishnani, Shafeeq Ladha, Pascal Laforêt, et al. “NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in participants with late-onset pompe disease (LOPD).” In Molecular Genetics and Metabolism, 132:S34–S34. Elsevier BV, 2021. https://doi.org/10.1016/j.ymgme.2020.12.064.
Dimachkie MM, Barohn RJ, Byrne B, Goker-Alpan O, Kishnani PS, Ladha S, et al. NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in participants with late-onset pompe disease (LOPD). In: Molecular Genetics and Metabolism. Elsevier BV; 2021. p. S34–S34.
Dimachkie, Mazen M., et al. “NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in participants with late-onset pompe disease (LOPD).” Molecular Genetics and Metabolism, vol. 132, no. 2, Elsevier BV, 2021, pp. S34–S34. Crossref, doi:10.1016/j.ymgme.2020.12.064.
Dimachkie MM, Barohn RJ, Byrne B, Goker-Alpan O, Kishnani PS, Ladha S, Laforêt P, Mengel KE, Pena LDM, Sacconi S, Straub V, Trivedi J, Van Damme P, van der Ploeg A, Vissing J, Young P, Haack KA, Ivanina I, Lu X, Benedikt Schoser; on behalf of NEO-EXT investigators. NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in participants with late-onset pompe disease (LOPD). Molecular Genetics and Metabolism. Elsevier BV; 2021. p. S34–S34.
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2021
Volume
132
Issue
2
Start / End Page
S34 / S34
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences