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Avalglucosidase alfa immunogenicity in alglucosidase alfa-experienced participants with Pompe disease: Pooled analysis of clinical trial data

Publication ,  Conference
Kishnani, PS; Richards, S; Al-Hassnan, ZN; Filosto, M; Hahn, A; Needham, M; Sacconi, S; van den Hout, H; Haack, KA; Miossec, P; Sparks, S ...
Published in: Molecular Genetics and Metabolism
February 2022

Duke Scholars

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2022

Volume

135

Issue

2

Start / End Page

S67 / S68

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences
 

Citation

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Kishnani, P. S., Richards, S., Al-Hassnan, Z. N., Filosto, M., Hahn, A., Needham, M., … Broomfield, A. (2022). Avalglucosidase alfa immunogenicity in alglucosidase alfa-experienced participants with Pompe disease: Pooled analysis of clinical trial data. In Molecular Genetics and Metabolism (Vol. 135, pp. S67–S68). Elsevier BV. https://doi.org/10.1016/j.ymgme.2021.11.169
Kishnani, Priya S., Susan Richards, Zuhair Nassair Al-Hassnan, Massimiliano Filosto, Andreas Hahn, Merrilee Needham, Sabrina Sacconi, et al. “Avalglucosidase alfa immunogenicity in alglucosidase alfa-experienced participants with Pompe disease: Pooled analysis of clinical trial data.” In Molecular Genetics and Metabolism, 135:S67–68. Elsevier BV, 2022. https://doi.org/10.1016/j.ymgme.2021.11.169.
Kishnani PS, Richards S, Al-Hassnan ZN, Filosto M, Hahn A, Needham M, et al. Avalglucosidase alfa immunogenicity in alglucosidase alfa-experienced participants with Pompe disease: Pooled analysis of clinical trial data. In: Molecular Genetics and Metabolism. Elsevier BV; 2022. p. S67–8.
Kishnani, Priya S., et al. “Avalglucosidase alfa immunogenicity in alglucosidase alfa-experienced participants with Pompe disease: Pooled analysis of clinical trial data.” Molecular Genetics and Metabolism, vol. 135, no. 2, Elsevier BV, 2022, pp. S67–68. Crossref, doi:10.1016/j.ymgme.2021.11.169.
Kishnani PS, Richards S, Al-Hassnan ZN, Filosto M, Hahn A, Needham M, Sacconi S, van den Hout H, Haack KA, Miossec P, Sparks S, Tammireddy S, Thibault N, Zhou T, Broomfield A. Avalglucosidase alfa immunogenicity in alglucosidase alfa-experienced participants with Pompe disease: Pooled analysis of clinical trial data. Molecular Genetics and Metabolism. Elsevier BV; 2022. p. S67–S68.
Journal cover image

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2022

Volume

135

Issue

2

Start / End Page

S67 / S68

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences