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Xiaoyan Li

Assistant Professor of Neurology
Neurology, Neuromuscular Disease

Current Appointments & Affiliations


Assistant Professor of Neurology · 2020 - Present Neurology, Neuromuscular Disease, Neurology

Recent Publications


ALSUntangled #81: Pyridostigmine (mestinon®).

Journal Article Amyotroph Lateral Scler Frontotemporal Degener · November 6, 2025 Pyridostigmine (Mestinon®, Bausch Health, Canada Inc.) increases acetylcholine availability at the neuromuscular junction, enhancing transmission. Preclinical studies suggest that neuromuscular junction dysfunction develops early in ALS, and pyridostigmine ... Full text Link to item Cite

Operational Development and Launch of an Adaptive Platform Trial in Amyotrophic Lateral Sclerosis: Processes and Learnings From the First Four Regimens of the HEALEY ALS Platform Trial.

Journal Article Muscle Nerve · August 2025 INTRODUCTION/AIMS: Platform trials present several advantages over traditional interventional clinical trials. Here, we provide a detailed description of the operational framework of the HEALEY ALS Platform Trial. METHODS: Platform-level procedures for reg ... Full text Link to item Cite

Safety and efficacy of trehalose in amyotrophic lateral sclerosis (HEALEY ALS Platform Trial): an adaptive, phase 2/3, double-blind, randomised, placebo-controlled trial.

Journal Article Lancet Neurol · June 2025 BACKGROUND: Trehalose is a disaccharide that activates autophagy pathways in animal models of neurodegenerative diseases, with the potential to catalyse clearance of toxic, misfolded proteins in motor neurons and slow disease progression in amyotrophic lat ... Full text Link to item Cite
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Recent Grants


ALL ALS Consortium - ASSESS Task Order

ResearchPrincipal Investigator · Awarded by MGH Institute of Health Professionals · 2024 - 2027

ALL ALS Consortium - PREVENT Task Order

ResearchPrincipal Investigator · Awarded by MGH Institute of Health Professionals · 2024 - 2027

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Education, Training & Certifications


Peking Union Medical College (China) · 2002 Ph.D.
Shandong Medical University (China) · 1999 M.S.
Taishan Medical University (China) · 1996 M.D.