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Elsevier BV

Comparison of infant versus adult treatment of murine Pompe disease with a recombinant AAV9 vector containing a minimal G6PC promoter

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Sun, B; Yi, H; Han, S-O; Li, S; Eisner, W; Brooks, ED; Bacon, R; Koeberl, DD
2026

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Publication Date

2026
 

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Sun, B., Yi, H., Han, S.-O., Li, S., Eisner, W., Brooks, E. D., … Koeberl, D. D. (2026). Comparison of infant versus adult treatment of murine Pompe disease with a recombinant AAV9 vector containing a minimal G6PC promoter. Elsevier BV. https://doi.org/10.2139/ssrn.6618082
Sun, Baodong, Haiqing Yi, Sang-oh Han, Songtao Li, William Eisner, Elizabeth D. Brooks, Rebecca Bacon, and Dwight D. Koeberl. “Comparison of infant versus adult treatment of murine Pompe disease with a recombinant AAV9 vector containing a minimal G6PC promoter.” Elsevier BV, 2026. https://doi.org/10.2139/ssrn.6618082.
Sun B, Yi H, Han S-O, Li S, Eisner W, Brooks ED, Bacon R, Koeberl DD. Comparison of infant versus adult treatment of murine Pompe disease with a recombinant AAV9 vector containing a minimal G6PC promoter. Elsevier BV. 2026.

DOI

Publication Date

2026