First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD)
Conferences
Rayes, A; Pulsipher, M; Ebens, C; Oved, J; Mousallem, T; Mahadeo, K; Kohn, D; Prockop, S; Dorsey, M; Leiding, J; Morris, EC; Shamir, E; Au, P ...
Published in: MOLECULAR THERAPY
May 8, 2026
Duke Scholars
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Published In
MOLECULAR THERAPY
EISSN
1525-0024
ISSN
1525-0016
Publication Date
May 8, 2026
Volume
34
Issue
5
Start / End Page
833 / 834
Related Subject Headings
- Biotechnology
- 3206 Medical biotechnology
- 3202 Clinical sciences
- 3105 Genetics
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Rayes, A., Pulsipher, M., Ebens, C., Oved, J., Mousallem, T., Mahadeo, K., … Malech, H. (2026). First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD). In MOLECULAR THERAPY (Vol. 34, pp. 833–834).
Rayes, Ahmad, Michael Pulsipher, Christen Ebens, Joseph Oved, Talal Mousallem, Kris Mahadeo, Donald Kohn, et al. “First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD).” In MOLECULAR THERAPY, 34:833–34, 2026.
Rayes A, Pulsipher M, Ebens C, Oved J, Mousallem T, Mahadeo K, et al. First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD). In: MOLECULAR THERAPY. 2026. p. 833–4.
Rayes, Ahmad, et al. “First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD).” MOLECULAR THERAPY, vol. 34, no. 5, 2026, pp. 833–34.
Rayes A, Pulsipher M, Ebens C, Oved J, Mousallem T, Mahadeo K, Kohn D, Prockop S, Dorsey M, Leiding J, Morris EC, Shamir E, Au P, Plescia C, Kiem H-P, Dietz AC, Booth C, Malech H. First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD). MOLECULAR THERAPY. 2026. p. 833–834.
Published In
MOLECULAR THERAPY
EISSN
1525-0024
ISSN
1525-0016
Publication Date
May 8, 2026
Volume
34
Issue
5
Start / End Page
833 / 834
Related Subject Headings
- Biotechnology
- 3206 Medical biotechnology
- 3202 Clinical sciences
- 3105 Genetics