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First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD)

Conferences
Rayes, A; Pulsipher, M; Ebens, C; Oved, J; Mousallem, T; Mahadeo, K; Kohn, D; Prockop, S; Dorsey, M; Leiding, J; Morris, EC; Shamir, E; Au, P ...
Published in: MOLECULAR THERAPY
May 8, 2026

Duke Scholars

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Published In

MOLECULAR THERAPY

EISSN

1525-0024

ISSN

1525-0016

Publication Date

May 8, 2026

Volume

34

Issue

5

Start / End Page

833 / 834

Related Subject Headings

  • Biotechnology
  • 3206 Medical biotechnology
  • 3202 Clinical sciences
  • 3105 Genetics
 

Citation

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Chicago
ICMJE
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Rayes, A., Pulsipher, M., Ebens, C., Oved, J., Mousallem, T., Mahadeo, K., … Malech, H. (2026). First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD). In MOLECULAR THERAPY (Vol. 34, pp. 833–834).
Rayes, Ahmad, Michael Pulsipher, Christen Ebens, Joseph Oved, Talal Mousallem, Kris Mahadeo, Donald Kohn, et al. “First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD).” In MOLECULAR THERAPY, 34:833–34, 2026.
Rayes A, Pulsipher M, Ebens C, Oved J, Mousallem T, Mahadeo K, et al. First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD). In: MOLECULAR THERAPY. 2026. p. 833–4.
Rayes A, Pulsipher M, Ebens C, Oved J, Mousallem T, Mahadeo K, Kohn D, Prockop S, Dorsey M, Leiding J, Morris EC, Shamir E, Au P, Plescia C, Kiem H-P, Dietz AC, Booth C, Malech H. First in vivo hematopoietic stem cell (HSC) gene addition clinical trial: Initial results from EN-374-101 in X-linked chronic granulomatous disease (X-CGD). MOLECULAR THERAPY. 2026. p. 833–834.

Published In

MOLECULAR THERAPY

EISSN

1525-0024

ISSN

1525-0016

Publication Date

May 8, 2026

Volume

34

Issue

5

Start / End Page

833 / 834

Related Subject Headings

  • Biotechnology
  • 3206 Medical biotechnology
  • 3202 Clinical sciences
  • 3105 Genetics