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Research
Genome editing for the correction of Pompe disease
Administered By
Pediatrics, Medical Genetics
Awarded By
National Institutes of Health
Contributors
Arnson, Benjamin
Graduate Student
Bursac, Nenad
Co Investigator
Koeberl, Dwight D.
Principal Investigator
Start/End
July 20, 2020 - June 30, 2022