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A Phase 3, Multinational, Randomized, Double-Blind, Placebo-Controlled Systemic Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of SRP-9001 in Non-Ambulatory and Ambulatory Subjects With Duchenne Muscular Dystrophy (ENVISION)

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Pulmonary and Sleep Medicine

Awarded By

Sarepta Therapeutics, Inc.

Start Date

August 8, 2023

End Date

March 12, 2026
 

Administered By

Pediatrics, Pulmonary and Sleep Medicine

Awarded By

Sarepta Therapeutics, Inc.

Start Date

August 8, 2023

End Date

March 12, 2026