A Phase 3, Multinational, Randomized, Double-Blind, Placebo-Controlled Systemic Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of SRP-9001 in Non-Ambulatory and Ambulatory Subjects With Duchenne Muscular Dystrophy (ENVISION)
Clinical Trial Grant
Administered By
Pediatrics, Pulmonary and Sleep Medicine
Awarded By
Sarepta Therapeutics, Inc.
Start Date
August 8, 2023
End Date
March 12, 2026
Administered By
Pediatrics, Pulmonary and Sleep Medicine
Awarded By
Sarepta Therapeutics, Inc.
Start Date
August 8, 2023
End Date
March 12, 2026