SUMMARY OF SCREENING DATA FROM 19 PATIENTS WITH LATE-ONSET POMPE DISEASE FOR A PHASE I CLINICAL TRIAL OF AAV VECTOR-MEDIATED GENE THERAPY

Published

Conference Paper

Full Text

Duke Authors

Cited Authors

  • Hannah, WB; Case, LE; Walters, C; Kishnani, PS; Koeberl, DD

Published Date

  • March 1, 2019

Published In

Volume / Issue

  • 126 / 3

Start / End Page

  • 305 - 306

Published By

Pages

  • 2

Electronic International Standard Serial Number (EISSN)

  • 1096-7206

International Standard Serial Number (ISSN)

  • 1096-7192

Conference Name

  • 41st Annual Meeting of the Society-for-Inherited-Metabolic-Disorders (SIMD)

Conference Location

  • Bellevue, WA

Conference Start Date

  • April 6, 2019

Conference End Date

  • April 9, 2019