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SUMMARY OF SCREENING DATA FROM 19 PATIENTS WITH LATE-ONSET POMPE DISEASE FOR A PHASE I CLINICAL TRIAL OF AAV VECTOR-MEDIATED GENE THERAPY

Publication ,  Conference
Hannah, WB; Case, LE; Walters, C; Kishnani, PS; Koeberl, DD
Published in: MOLECULAR GENETICS AND METABOLISM
July 1, 2019

Duke Scholars

Published In

MOLECULAR GENETICS AND METABOLISM

EISSN

1096-7206

ISSN

1096-7192

Publication Date

July 1, 2019

Volume

127

Issue

3

Start / End Page

274 / 274

Location

Bellevue, WA

Publisher

ACADEMIC PRESS INC ELSEVIER SCIENCE

Conference Name

41st Annual Meeting of the Society-for-Inherited-Metabolic-Disorders (SIMD)

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences
 

Citation

APA
Chicago
ICMJE
MLA
NLM
Hannah, W. B., Case, L. E., Walters, C., Kishnani, P. S., & Koeberl, D. D. (2019). SUMMARY OF SCREENING DATA FROM 19 PATIENTS WITH LATE-ONSET POMPE DISEASE FOR A PHASE I CLINICAL TRIAL OF AAV VECTOR-MEDIATED GENE THERAPY. In MOLECULAR GENETICS AND METABOLISM (Vol. 127, pp. 274–274). Bellevue, WA: ACADEMIC PRESS INC ELSEVIER SCIENCE.
Hannah, William B., Laura E. Case, Crista Walters, Priya S. Kishnani, and Dwight D. Koeberl. “SUMMARY OF SCREENING DATA FROM 19 PATIENTS WITH LATE-ONSET POMPE DISEASE FOR A PHASE I CLINICAL TRIAL OF AAV VECTOR-MEDIATED GENE THERAPY.” In MOLECULAR GENETICS AND METABOLISM, 127:274–274. ACADEMIC PRESS INC ELSEVIER SCIENCE, 2019.
Hannah WB, Case LE, Walters C, Kishnani PS, Koeberl DD. SUMMARY OF SCREENING DATA FROM 19 PATIENTS WITH LATE-ONSET POMPE DISEASE FOR A PHASE I CLINICAL TRIAL OF AAV VECTOR-MEDIATED GENE THERAPY. In: MOLECULAR GENETICS AND METABOLISM. ACADEMIC PRESS INC ELSEVIER SCIENCE; 2019. p. 274–274.
Hannah, William B., et al. “SUMMARY OF SCREENING DATA FROM 19 PATIENTS WITH LATE-ONSET POMPE DISEASE FOR A PHASE I CLINICAL TRIAL OF AAV VECTOR-MEDIATED GENE THERAPY.” MOLECULAR GENETICS AND METABOLISM, vol. 127, no. 3, ACADEMIC PRESS INC ELSEVIER SCIENCE, 2019, pp. 274–274.
Hannah WB, Case LE, Walters C, Kishnani PS, Koeberl DD. SUMMARY OF SCREENING DATA FROM 19 PATIENTS WITH LATE-ONSET POMPE DISEASE FOR A PHASE I CLINICAL TRIAL OF AAV VECTOR-MEDIATED GENE THERAPY. MOLECULAR GENETICS AND METABOLISM. ACADEMIC PRESS INC ELSEVIER SCIENCE; 2019. p. 274–274.
Journal cover image

Published In

MOLECULAR GENETICS AND METABOLISM

EISSN

1096-7206

ISSN

1096-7192

Publication Date

July 1, 2019

Volume

127

Issue

3

Start / End Page

274 / 274

Location

Bellevue, WA

Publisher

ACADEMIC PRESS INC ELSEVIER SCIENCE

Conference Name

41st Annual Meeting of the Society-for-Inherited-Metabolic-Disorders (SIMD)

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences