Developing a management approach for patients with the "late-onset" Pompe disease GAA variant identified by newborn screening
Research Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Amicus Therapeutics Corporation
Start Date
November 29, 2018
End Date
March 31, 2022
Administered By
Pediatrics, Medical Genetics
Awarded By
Amicus Therapeutics Corporation
Start Date
November 29, 2018
End Date
March 31, 2022