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Developing a management approach for patients with the "late-onset" Pompe disease GAA variant identified by newborn screening

Research Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Amicus Therapeutics Corporation

Start Date

November 29, 2018

End Date

March 31, 2022
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Amicus Therapeutics Corporation

Start Date

November 29, 2018

End Date

March 31, 2022