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A Phase 1 Study of AAV8-LSPhGAA (ACTUS-101) in Late-Onset Pompe Disease

Clinical Trial Grant
Duke Scholars

Awarded By

Actus Therapeutics

Start Date

November 20, 2018

End Date

November 30, 2024
 

Awarded By

Actus Therapeutics

Start Date

November 20, 2018

End Date

November 30, 2024