A Randomized, Double-Blind, Placebo-Controlled, Multicenter, Seamless, Adaptive, Safety, Dose-Finding, and Phase 3 Clinical Study of UX701 AAV-Mediated Gene Transfer for the Treatment of Wilson Disease
Clinical Trial Grant
Administered By
Medicine, Gastroenterology
Awarded By
Ultragenyx Pharmaceutical
Start Date
February 9, 2022
End Date
February 27, 2027
Administered By
Medicine, Gastroenterology
Awarded By
Ultragenyx Pharmaceutical
Start Date
February 9, 2022
End Date
February 27, 2027