Skeletal muscle-targeted gene therapy for Pompe disease

Research Grant

Duke Scholars

Co Investigator Dwight D. Koeberl Pediatrics, Medical Genetics

Co Investigator Sarah Phyllis Young Pediatrics, Medical Genetics

Co Investigator Beatrice Edith Monique Bissig-Choisat Pediatrics, Medical Genetics

Principal Investigator Baodong Sun Pediatrics, Medical Genetics

Co Investigator Karl-Dimiter Bissig Pediatrics, Medical Genetics

Administered By

Pediatrics

Awarded By

National Institute of Arthritis and Musculoskeletal and Skin Diseases

Start Date

September 1, 2025

End Date

August 31, 2030

Administered By

Pediatrics

Awarded By

National Institute of Arthritis and Musculoskeletal and Skin Diseases

Start Date

September 1, 2025

End Date

August 31, 2030