Selected Grants
Developing strategies to identify candidate individuals for early genetic therapies
ResearchPrincipal Investigator · Awarded by Eunice Kennedy Shriver National Institute of Child Health and Human Development · 2024 - 2029An Open-label, Dose-Finding, Phase 1/2 Study to Evaluate the Safety and Tolerability of a Single Intravenous Dose of LY3884961 in Patients with Peripheral Manifestations of Gaucher Disease
Clinical TrialPrincipal Investigator · Awarded by Lilly USA, LLC · 2023 - 2026Phase 1 Study of In Utero Enzyme Replacement Therapy for the Treatment of Lysosomal Storage Diseases
ResearchPrincipal Investigator · Awarded by University of California - San Francisco · 2022 - 2026Fellowships, Gifts, and Supported Research
Analyzing clinical and immunological outcomes of early postnatal treatment for lysosomal storage diseases ·
April 2021
Awarded by: Duke Children’s Health and Discovery Initiative (CHDI)
External Relationships
- Bayer Healthcare Pharmaceuticals
- Sanofi Genzyme
This faculty member (or a member of their immediate family) has reported outside activities with the companies, institutions, or organizations listed above. This information is available to institutional leadership and, when appropriate, management plans are in place to address potential conflicts of interest.