Overview
Bone Marrow Failure Syndromes
General Hematology
Current Appointments & Affiliations
Professor of Pediatrics
·
2022 - Present
Pediatrics, Hematology-Oncology,
Pediatrics
Professor in Medicine
·
2022 - Present
Medicine, Hematology,
Medicine
Recent Publications
Eltrombopag in combination with immunosuppressive therapy in pediatric severe aplastic anemia: Phase 2 ESCALATE trial.
Journal Article Blood Adv · May 2, 2025 Severe aplastic anemia (SAA) is a rare, life-threatening disease with acquired pancytopenia and hypocellular bone marrow. ESCALATE evaluated eltrombopag in combination with immunosuppressive therapy (IST) in pediatric patients (aged 1 to <18 years) with re ... Full text Link to item CiteWorking toward international consensus defining pediatric "refractory ITP".
Journal Article Blood Adv · March 11, 2025 Full text Link to item CiteMulticenter comparative study of polysomnography outcomes in children with the monogenic disorder sickle cell disease.
Journal Article J Clin Sleep Med · February 1, 2025 STUDY OBJECTIVES: Sleep-disordered breathing is prevalent in children with sickle cell disease (SCD) and is associated with worse outcomes. This study aimed to compare the outcomes of polysomnography (PSG) performed for pediatric patients with SCD at 3 US ... Full text Link to item CiteRecent Grants
A global phase 3, randomised, double-blind and placebo-controlled study evaluating the efficacy and safety of etavopivat in adolescents and adults with sickle cell disease
Clinical TrialPrincipal Investigator · Awarded by Novo Nordisk, Inc. · 2025 - 2027Achieving Understanding of the Natural history of sickle cell Trait (AUNT)
ResearchCollaborating Investigator · Awarded by National Alliance for Sickle Cell Centers · 2024 - 2026A Phase 3 Study of Eltrombopag vs. Standard First-Line Management for Newly Diagnosed Immune Thrombocytopenia (ITP) in Children
Clinical TrialPrincipal Investigator · Awarded by Novartis Pharmaceuticals Corporation · 2019 - 2026View All Grants
Education, Training & Certifications
University of Medicine and Dentistry of New Jersey ·
2003
M.D.