In the News

Published November 10, 2022
Duke Experts Participate in First Use of Fetal Therapy for Pompe Disease

Published January 26, 2017
Gene Therapy for Pompe Disease Effective in Mice, Poised for Human Trials

Published January 28, 2014
Dr. Priya Kishnani comments: Agonizing choices for lives saved by miracle drugs

Published November 21, 2013
Dr. Priya Kishnani comments: Genetic testing leaves more patients living in limbo

Published August 19, 2013
‘Miracle in Motion’: Children with Pompe disease unite during Duke reunion