Chien, Y.-H., van der Ploeg, A., Jones, S. A., Byrne, B., Vellodi, A., Leslie, N., … Kishnani, P. S. (2014). Survival and developmental milestones among Pompe registry patients with classic infantile-onset Pompe disease with different timing of initiation of treatment with enzyme replacement therapy (ERT). In Molecular Genetics and Metabolism (Vol. 111, pp. S31–S32). Elsevier BV. https://doi.org/10.1016/j.ymgme.2013.12.057

Chien, Yin-Hsiu, Ans van der Ploeg, Simon A. Jones, Barry Byrne, Ashok Vellodi, Nancy Leslie, Eugen Mengel, et al. “Survival and developmental milestones among Pompe registry patients with classic infantile-onset Pompe disease with different timing of initiation of treatment with enzyme replacement therapy (ERT).” In Molecular Genetics and Metabolism, 111:S31–32. Elsevier BV, 2014. https://doi.org/10.1016/j.ymgme.2013.12.057.

Chien Y-H, van der Ploeg A, Jones SA, Byrne B, Vellodi A, Leslie N, et al. Survival and developmental milestones among Pompe registry patients with classic infantile-onset Pompe disease with different timing of initiation of treatment with enzyme replacement therapy (ERT). In: Molecular Genetics and Metabolism. Elsevier BV; 2014. p. S31–2.

Chien, Yin-Hsiu, et al. “Survival and developmental milestones among Pompe registry patients with classic infantile-onset Pompe disease with different timing of initiation of treatment with enzyme replacement therapy (ERT).” Molecular Genetics and Metabolism, vol. 111, no. 2, Elsevier BV, 2014, pp. S31–32. Crossref, doi:10.1016/j.ymgme.2013.12.057.

Chien Y-H, van der Ploeg A, Jones SA, Byrne B, Vellodi A, Leslie N, Mengel E, Shankar S, Tanpaiboon P, Stockton DW, Hennermann JB, Devecseri Z, Kempf J, Keutzer J, Kishnani PS. Survival and developmental milestones among Pompe registry patients with classic infantile-onset Pompe disease with different timing of initiation of treatment with enzyme replacement therapy (ERT). Molecular Genetics and Metabolism. Elsevier BV; 2014. p. S31–S32.