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52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study

Publication ,  Conference
Hahn, S; Pena, L; Day, JW; Gambello, M; Gibson, JB; Hillman, R; Kronn, D; Stockton, D; Leslie, N; Tanpaiboon, P; Wang, R; Haack, KA; Zhao, Y ...
Published in: Molecular Genetics and Metabolism
February 2016

Duke Scholars

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2016

Volume

117

Issue

2

Start / End Page

S54 / S54

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences
 

Citation

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Hahn, S., Pena, L., Day, J. W., Gambello, M., Gibson, J. B., Hillman, R., … Kishnani, P. S. (2016). 52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study. In Molecular Genetics and Metabolism (Vol. 117, pp. S54–S54). Elsevier BV. https://doi.org/10.1016/j.ymgme.2015.12.281
Hahn, Sihoun, Loren Pena, John W. Day, Michael Gambello, James B. Gibson, Richard Hillman, David Kronn, et al. “52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study.” In Molecular Genetics and Metabolism, 117:S54–S54. Elsevier BV, 2016. https://doi.org/10.1016/j.ymgme.2015.12.281.
Hahn S, Pena L, Day JW, Gambello M, Gibson JB, Hillman R, et al. 52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study. In: Molecular Genetics and Metabolism. Elsevier BV; 2016. p. S54–S54.
Hahn, Sihoun, et al. “52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study.” Molecular Genetics and Metabolism, vol. 117, no. 2, Elsevier BV, 2016, pp. S54–S54. Crossref, doi:10.1016/j.ymgme.2015.12.281.
Hahn S, Pena L, Day JW, Gambello M, Gibson JB, Hillman R, Kronn D, Stockton D, Leslie N, Tanpaiboon P, Wang R, Haack KA, Sparks S, Zhao Y, Kishnani PS. 52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study. Molecular Genetics and Metabolism. Elsevier BV; 2016. p. S54–S54.
Journal cover image

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2016

Volume

117

Issue

2

Start / End Page

S54 / S54

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences