52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study
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Hahn, S; Pena, L; Day, JW; Gambello, M; Gibson, JB; Hillman, R; Kronn, D; Stockton, D; Leslie, N; Tanpaiboon, P; Wang, R; Haack, KA; Zhao, Y ...
Published in: Molecular Genetics and Metabolism
February 2016
Duke Scholars
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2016
Volume
117
Issue
2
Start / End Page
S54 / S54
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences
Citation
APA
Chicago
ICMJE
MLA
NLM
Hahn, S., Pena, L., Day, J. W., Gambello, M., Gibson, J. B., Hillman, R., … Kishnani, P. S. (2016). 52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study. In Molecular Genetics and Metabolism (Vol. 117, pp. S54–S54). Elsevier BV. https://doi.org/10.1016/j.ymgme.2015.12.281
Hahn, Sihoun, Loren Pena, John W. Day, Michael Gambello, James B. Gibson, Richard Hillman, David Kronn, et al. “52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study.” In Molecular Genetics and Metabolism, 117:S54–S54. Elsevier BV, 2016. https://doi.org/10.1016/j.ymgme.2015.12.281.
Hahn S, Pena L, Day JW, Gambello M, Gibson JB, Hillman R, et al. 52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study. In: Molecular Genetics and Metabolism. Elsevier BV; 2016. p. S54–S54.
Hahn, Sihoun, et al. “52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study.” Molecular Genetics and Metabolism, vol. 117, no. 2, Elsevier BV, 2016, pp. S54–S54. Crossref, doi:10.1016/j.ymgme.2015.12.281.
Hahn S, Pena L, Day JW, Gambello M, Gibson JB, Hillman R, Kronn D, Stockton D, Leslie N, Tanpaiboon P, Wang R, Haack KA, Sparks S, Zhao Y, Kishnani PS. 52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study. Molecular Genetics and Metabolism. Elsevier BV; 2016. p. S54–S54.
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2016
Volume
117
Issue
2
Start / End Page
S54 / S54
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences