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FIRST-IN-HUMAN STUDY OF AT-GAA (ATB200/AT2221) IN PATIENTS WITH POMPE DISEASE: PRELIMINARY RESULTS FROM THE ATB200-02 TRIAL

Publication ,  Conference
Mozaffar, T; Bratkovic, D; Byrne, BJ; Clemens, P; Geberhiwot, T; Goker-Alpan, O; Kishnani, P; Ming, X; Roberts, M; Schwenkreis, P; Sivakumar, K ...
Published in: MUSCLE & NERVE
September 1, 2018

Duke Scholars

Published In

MUSCLE & NERVE

EISSN

1097-4598

ISSN

0148-639X

Publication Date

September 1, 2018

Volume

58

Start / End Page

S1 / S1

Location

Oxford, ENGLAND

Publisher

WILEY

Conference Name

Annual Scientific Meeting of the Muscle-Study-Group - The Changing Landscape of NeuroMuscular Disease - The Future is Here

Related Subject Headings

  • Neurology & Neurosurgery
  • 32 Biomedical and clinical sciences
  • 31 Biological sciences
  • 11 Medical and Health Sciences
 

Citation

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MLA
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Mozaffar, T., Bratkovic, D., Byrne, B. J., Clemens, P., Geberhiwot, T., Goker-Alpan, O., … Schoser, B. (2018). FIRST-IN-HUMAN STUDY OF AT-GAA (ATB200/AT2221) IN PATIENTS WITH POMPE DISEASE: PRELIMINARY RESULTS FROM THE ATB200-02 TRIAL. In MUSCLE & NERVE (Vol. 58, pp. S1–S1). Oxford, ENGLAND: WILEY.
Mozaffar, T., D. Bratkovic, B. J. Byrne, P. Clemens, T. Geberhiwot, O. Goker-Alpan, P. Kishnani, et al. “FIRST-IN-HUMAN STUDY OF AT-GAA (ATB200/AT2221) IN PATIENTS WITH POMPE DISEASE: PRELIMINARY RESULTS FROM THE ATB200-02 TRIAL.” In MUSCLE & NERVE, 58:S1–S1. WILEY, 2018.
Mozaffar T, Bratkovic D, Byrne BJ, Clemens P, Geberhiwot T, Goker-Alpan O, et al. FIRST-IN-HUMAN STUDY OF AT-GAA (ATB200/AT2221) IN PATIENTS WITH POMPE DISEASE: PRELIMINARY RESULTS FROM THE ATB200-02 TRIAL. In: MUSCLE & NERVE. WILEY; 2018. p. S1–S1.
Mozaffar T, Bratkovic D, Byrne BJ, Clemens P, Geberhiwot T, Goker-Alpan O, Kishnani P, Ming X, Roberts M, Schwenkreis P, Sivakumar K, van der Ploeg AT, Wright J, Johnson FK, Sitaraman S, Barth JA, Sathe S, Schoser B. FIRST-IN-HUMAN STUDY OF AT-GAA (ATB200/AT2221) IN PATIENTS WITH POMPE DISEASE: PRELIMINARY RESULTS FROM THE ATB200-02 TRIAL. MUSCLE & NERVE. WILEY; 2018. p. S1–S1.
Journal cover image

Published In

MUSCLE & NERVE

EISSN

1097-4598

ISSN

0148-639X

Publication Date

September 1, 2018

Volume

58

Start / End Page

S1 / S1

Location

Oxford, ENGLAND

Publisher

WILEY

Conference Name

Annual Scientific Meeting of the Muscle-Study-Group - The Changing Landscape of NeuroMuscular Disease - The Future is Here

Related Subject Headings

  • Neurology & Neurosurgery
  • 32 Biomedical and clinical sciences
  • 31 Biological sciences
  • 11 Medical and Health Sciences