EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL)
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, Conference
Byrne, BJ; Bratkovic, D; Laforet, P; Mozaffar, T; van der Ploeg, A; Roberts, M; Schoser, B; Toscano, A; Jiang, H; Sitaraman, S; Kuchipudi, S ...
Published in: MUSCLE & NERVE
2021
Duke Scholars
Published In
MUSCLE & NERVE
EISSN
1097-4598
ISSN
0148-639X
Publication Date
2021
Volume
64
Start / End Page
S64 / S65
Related Subject Headings
- Neurology & Neurosurgery
- 32 Biomedical and clinical sciences
- 31 Biological sciences
- 11 Medical and Health Sciences
Citation
APA
Chicago
ICMJE
MLA
NLM
Byrne, B. J., Bratkovic, D., Laforet, P., Mozaffar, T., van der Ploeg, A., Roberts, M., … Kishnani, P. S. (2021). EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL). In MUSCLE & NERVE (Vol. 64, pp. S64–S65).
Byrne, Barry J., Drago Bratkovic, Pascal Laforet, Tahseen Mozaffar, Ans van der Ploeg, Mark Roberts, Benedikt Schoser, et al. “EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL).” In MUSCLE & NERVE, 64:S64–65, 2021.
Byrne BJ, Bratkovic D, Laforet P, Mozaffar T, van der Ploeg A, Roberts M, et al. EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL). In: MUSCLE & NERVE. 2021. p. S64–5.
Byrne, Barry J., et al. “EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL).” MUSCLE & NERVE, vol. 64, 2021, pp. S64–65.
Byrne BJ, Bratkovic D, Laforet P, Mozaffar T, van der Ploeg A, Roberts M, Schoser B, Toscano A, Jiang H, Sitaraman S, Kuchipudi S, Kazi Z, Goldman M, Castelli J, Kishnani PS. EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL). MUSCLE & NERVE. 2021. p. S64–S65.
Published In
MUSCLE & NERVE
EISSN
1097-4598
ISSN
0148-639X
Publication Date
2021
Volume
64
Start / End Page
S64 / S65
Related Subject Headings
- Neurology & Neurosurgery
- 32 Biomedical and clinical sciences
- 31 Biological sciences
- 11 Medical and Health Sciences