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EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL)

Publication ,  Conference
Byrne, BJ; Bratkovic, D; Laforet, P; Mozaffar, T; van der Ploeg, A; Roberts, M; Schoser, B; Toscano, A; Jiang, H; Sitaraman, S; Kuchipudi, S ...
Published in: MUSCLE & NERVE
2021

Duke Scholars

Published In

MUSCLE & NERVE

EISSN

1097-4598

ISSN

0148-639X

Publication Date

2021

Volume

64

Start / End Page

S64 / S65

Related Subject Headings

  • Neurology & Neurosurgery
  • 32 Biomedical and clinical sciences
  • 31 Biological sciences
  • 11 Medical and Health Sciences
 

Citation

APA
Chicago
ICMJE
MLA
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Byrne, B. J., Bratkovic, D., Laforet, P., Mozaffar, T., van der Ploeg, A., Roberts, M., … Kishnani, P. S. (2021). EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL). In MUSCLE & NERVE (Vol. 64, pp. S64–S65).
Byrne, Barry J., Drago Bratkovic, Pascal Laforet, Tahseen Mozaffar, Ans van der Ploeg, Mark Roberts, Benedikt Schoser, et al. “EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL).” In MUSCLE & NERVE, 64:S64–65, 2021.
Byrne BJ, Bratkovic D, Laforet P, Mozaffar T, van der Ploeg A, Roberts M, et al. EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL). In: MUSCLE & NERVE. 2021. p. S64–5.
Byrne BJ, Bratkovic D, Laforet P, Mozaffar T, van der Ploeg A, Roberts M, Schoser B, Toscano A, Jiang H, Sitaraman S, Kuchipudi S, Kazi Z, Goldman M, Castelli J, Kishnani PS. EFFICACY AND SAFETY OF CIPAGLUCOSIDASE ALFA/MIGLUSTAT VERSUS ALGLUCOSIDASE ALFA/PLACEBO IN LATE-ONSET POMPE DISEASE: A PHASE 3 TRIAL (PROPEL). MUSCLE & NERVE. 2021. p. S64–S65.
Journal cover image

Published In

MUSCLE & NERVE

EISSN

1097-4598

ISSN

0148-639X

Publication Date

2021

Volume

64

Start / End Page

S64 / S65

Related Subject Headings

  • Neurology & Neurosurgery
  • 32 Biomedical and clinical sciences
  • 31 Biological sciences
  • 11 Medical and Health Sciences