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In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation.

Publication ,  Journal Article
Moreno, AM; Fu, X; Zhu, J; Katrekar, D; Shih, Y-RV; Marlett, J; Cabotaje, J; Tat, J; Naughton, J; Lisowski, L; Varghese, S; Zhang, K; Mali, P
Published in: Mol Ther
August 5, 2020

Duke Scholars

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Published In

Mol Ther

DOI

EISSN

1525-0024

Publication Date

August 5, 2020

Volume

28

Issue

8

Start / End Page

1931

Location

United States

Related Subject Headings

  • Biotechnology
  • 3206 Medical biotechnology
  • 3202 Clinical sciences
  • 3105 Genetics
  • 11 Medical and Health Sciences
  • 10 Technology
  • 06 Biological Sciences
 

Citation

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Moreno, A. M., Fu, X., Zhu, J., Katrekar, D., Shih, Y.-R., Marlett, J., … Mali, P. (2020). In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation. Mol Ther, 28(8), 1931. https://doi.org/10.1016/j.ymthe.2020.06.027
Moreno, Ana M., Xin Fu, Jie Zhu, Dhruva Katrekar, Yu-Ru V. Shih, John Marlett, Jessica Cabotaje, et al. “In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation.Mol Ther 28, no. 8 (August 5, 2020): 1931. https://doi.org/10.1016/j.ymthe.2020.06.027.
Moreno AM, Fu X, Zhu J, Katrekar D, Shih Y-RV, Marlett J, et al. In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation. Mol Ther. 2020 Aug 5;28(8):1931.
Moreno, Ana M., et al. “In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation.Mol Ther, vol. 28, no. 8, Aug. 2020, p. 1931. Pubmed, doi:10.1016/j.ymthe.2020.06.027.
Moreno AM, Fu X, Zhu J, Katrekar D, Shih Y-RV, Marlett J, Cabotaje J, Tat J, Naughton J, Lisowski L, Varghese S, Zhang K, Mali P. In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation. Mol Ther. 2020 Aug 5;28(8):1931.

Published In

Mol Ther

DOI

EISSN

1525-0024

Publication Date

August 5, 2020

Volume

28

Issue

8

Start / End Page

1931

Location

United States

Related Subject Headings

  • Biotechnology
  • 3206 Medical biotechnology
  • 3202 Clinical sciences
  • 3105 Genetics
  • 11 Medical and Health Sciences
  • 10 Technology
  • 06 Biological Sciences