Research Interests
Virology
RNA Biology
Viral Engineering
RNA Engineering
Gene Therapy
Gene Editing
Gene Regulation
Regenerative Medicine
RNA Biology
Viral Engineering
RNA Engineering
Gene Therapy
Gene Editing
Gene Regulation
Regenerative Medicine
Selected Grants
Enhancing limb regeneration with gene therapy informed by comparative biology
ResearchCollaborator · Awarded by National Institutes of Health · 2024 - 2029Optimizing Gene Therapy for Respiratory Insufficiency in Duchenne Muscular Dystrophy
ResearchCo Investigator · Awarded by National Institutes of Health · 2024 - 2028Determinants of AAV Tropism
ResearchPrincipal Investigator · Awarded by National Institutes of Health · 2008 - 2028University Training Program in Biomolecular and Tissue Engineering
Inst. Training Prgm or CMEMentor · Awarded by National Institutes of Health · 1994 - 2027Engineering cellular secretion for gene delivery
ResearchPrincipal Investigator · Awarded by National Institute of Biomedical Imaging and Bioengineering · 2023 - 2027Enhancing limb regeneration with gene therapy informed by comparative biology
ResearchCollaborator · Awarded by National Institutes of Health · 2024 - 2029Optimizing Gene Therapy for Respiratory Insufficiency in Duchenne Muscular Dystrophy
ResearchCo Investigator · Awarded by National Institutes of Health · 2024 - 2028Determinants of AAV Tropism
ResearchPrincipal Investigator · Awarded by National Institutes of Health · 2008 - 2028University Training Program in Biomolecular and Tissue Engineering
Inst. Training Prgm or CMEMentor · Awarded by National Institutes of Health · 1994 - 2027Engineering cellular secretion for gene delivery
ResearchPrincipal Investigator · Awarded by National Institute of Biomedical Imaging and Bioengineering · 2023 - 2027Genetic engineering of kidney allografts by ex vivo perfusion delivery of adeno-associated viral vectors
ResearchCo-Principal Investigator · Awarded by National Institute of Allergy and Infectious Diseases · 2022 - 2027Gene therapy for glycogen storage disease type III
ResearchCo Investigator · Awarded by National Institutes of Health · 2022 - 2027Dissecting AAV silencing in humanized mice
ResearchCo-Principal Investigator · Awarded by National Institutes of Health · 2023 - 2027Myovascular Mechanisms of Cardiac Growth and Regeneration
ResearchCollaborator · Awarded by National Institutes of Health · 2022 - 2026Preclinical Development of Gene Replacement Therapy Using Novel AV Vectors in Familial Cerebral Cavernous Malformations
ResearchCo Investigator · Awarded by Department of Defense · 2023 - 2026Interdisciplinary Research Training Program in AIDS
Inst. Training Prgm or CMEAdvisor · Awarded by National Institutes of Health · 2010 - 2025Evaluation of adeno-associated viral (AAV) mediated gene replacement therapy as a therapeutic option for SLC25A4 deficiency
FellowshipPrincipal Investigator · Awarded by National Heart, Lung, and Blood Institute · 2023 - 2025Evolving novel AAV vectors for gene therapy to cure HIV
ResearchPrincipal Investigator · Awarded by Oregon Health & Science University · 2022 - 2025Evaluating Wnt-Modulators as a Therapy for Treatment of Arrhythmic Cardiomyopathy In Vivo
ResearchCollaborator · Awarded by Hartwell Foundation · 2022 - 2025Reduction of Brain AVM Severity through Inhibition of Pathogenic Angiogenesis
ResearchPrincipal Investigator · Awarded by University of California - San Francisco · 2020 - 2025Liver-directed AAV gene therapy for PHKG2-Glycogen Storage Disease IX (GSD IX y2)
FellowshipCo-Sponsor · Awarded by National Institutes of Health · 2021 - 2024Evolving High Potency AAV Vectors for Neuromuscular Genome Editing
ResearchPrincipal Investigator · Awarded by National Institutes of Health · 2018 - 2024AAV gene therapy for the treatment of Glycogen Storage Disease IX y2
ResearchInvestigator · Awarded by Kriya Therapeutics · 2022 - 2024Targeted Therapy for Pompe Disease
ResearchCo Investigator · Awarded by National Institutes of Health · 2019 - 2024LUMICKS C-TRAP
EquipmentMajor User · Awarded by National Institutes of Health · 2022 - 2023Epigenome Editing Technologies for Treating Diverse Disease
ResearchCo Investigator · Awarded by National Institutes of Health · 2019 - 2023AAV-Exosomes: Escaping Neutralizing Antibody and Enhancing Delivery
ResearchPrincipal Investigator · Awarded by Icahn School of Medicine at Mount Sinai · 2019 - 2023Next Generation AAV Vectors for Kidney Gene Therapy
ResearchPrincipal Investigator · Awarded by BridgeBio Gene Therapy Research, Inc. · 2021 - 2023Editing the Kidney Epigenome
ResearchCo Investigator · Awarded by University of Washington · 2021 - 2022CircRNAs and CNS Gene Transfer
ResearchPrincipal Investigator · Awarded by National Institutes of Health · 2018 - 2022RE-ENGINEERING AAV GENOME PACKAGING
ResearchPrincipal Investigator · Awarded by National Institutes of Health · 2018 - 2022Characterization of Recombinant Adeno-Associated Viral Vectors
ResearchPrincipal Investigator · Awarded by StrideBio LLC · 2019 - 2022CRISPR/Cas9-Based Gene Editing for the Correction of Duchenne Muscular Dystrophy
ResearchCo Investigator · Awarded by National Institutes of Health · 2016 - 2021NONHUMAN PRIMATE TESTING CENTER FOR EVALUATION OF SOMATIC CELL GENOME EDITING TOOLS
ResearchPrincipal Investigator · Awarded by University of California - Davis · 2019 - 2020External Relationships
- Atsena Therapeutics
- Coave Therapeutics
- Ginkgo Bioworks
- Kriya Therapeutics, Inc.
- Lucidigm Therapeutics
- Atsena Therapeutics
- Coave Therapeutics
- Ginkgo Bioworks
- Kriya Therapeutics, Inc.
- Lucidigm Therapeutics
- Mammoth Biosciences Inc
- Nvelop Therapeutics
- Ring Therapeutics
- Sphere Gene Therapeutics, Inc
- TorqueBio Inc
This faculty member (or a member of their immediate family) has reported outside activities with the companies, institutions, or organizations listed above. This information is available to institutional leadership and, when appropriate, management plans are in place to address potential conflicts of interest.