Chonat, S., Grace, R., Dickerson, K., Andres, O., Bartels, M., Beynon, V., … Sevilla, J. (2025). Efficacy and safety of mitapivat in pediatric patients with pyruvate kinase deficiency who are not regularly transfused: Results from the Phase 3, global, randomized, double-blind, placebo-controlled ACTIVATE-Kids trial. In Blood (Vol. 146, pp. 4654–4654). American Society of Hematology. https://doi.org/10.1182/blood-2025-4654

Chonat, Satheesh, Rachael Grace, Kathryn Dickerson, Oliver Andres, Marije Bartels, Vanessa Beynon, Jenny Despotovic, et al. “Efficacy and safety of mitapivat in pediatric patients with pyruvate kinase deficiency who are not regularly transfused: Results from the Phase 3, global, randomized, double-blind, placebo-controlled ACTIVATE-Kids trial.” In Blood, 146:4654–4654. American Society of Hematology, 2025. https://doi.org/10.1182/blood-2025-4654.

Chonat S, Grace R, Dickerson K, Andres O, Bartels M, Beynon V, et al. Efficacy and safety of mitapivat in pediatric patients with pyruvate kinase deficiency who are not regularly transfused: Results from the Phase 3, global, randomized, double-blind, placebo-controlled ACTIVATE-Kids trial. In: Blood. American Society of Hematology; 2025. p. 4654–4654.

Chonat, Satheesh, et al. “Efficacy and safety of mitapivat in pediatric patients with pyruvate kinase deficiency who are not regularly transfused: Results from the Phase 3, global, randomized, double-blind, placebo-controlled ACTIVATE-Kids trial.” Blood, vol. 146, no. Supplement 1, American Society of Hematology, 2025, pp. 4654–4654. Crossref, doi:10.1182/blood-2025-4654.

Chonat S, Grace R, Dickerson K, Andres O, Bartels M, Beynon V, Despotovic J, Glader B, Huguenin Y, Kwiatkowski J, Laflam E, Rivadeneyra L, McGee B, Yin O, Murciano Carrillo T, Pastore Y, Rothman J, Tyler P, Xu E, Renella R, Sevilla J. Efficacy and safety of mitapivat in pediatric patients with pyruvate kinase deficiency who are not regularly transfused: Results from the Phase 3, global, randomized, double-blind, placebo-controlled ACTIVATE-Kids trial. Blood. American Society of Hematology; 2025. p. 4654–4654.