A Phase I Study of the Safety of AAV2/8 LSPhGAA in Late-onset Pompe Disease
Administered By
Awarded By
Contributors
- Bali, Deeksha Sarihyan Co Investigator
- Bond, Jennifer Program Leader
- Case, Laura Elizabeth Co Investigator
- ElMallah, Mai Co Investigator
- Hornik, Christoph Paul Vincent Co Investigator
- Kishnani, Priya Sunil Co Investigator
- Koeberl, Dwight D. Principal Investigator
- Smith, Edward Clinton Co Investigator
- Young, Sarah Phyllis Co Investigator
Start/End
- September 5, 2017 - June 30, 2020