Correction of biochemical abnormalities and gene expression associated with improved muscle function in a phase I/II clinical trial of clenbuterol in Pompe disease patients stably treated with ERT
Publication
, Conference
Koeberl, D; Case, L; Smith, EC; Li, Y; Walters, C; Hornik, C; Thurberg, B; Bali, D; Bursac, N; Kishnani, PS
Published in: Molecular Genetics and Metabolism
February 2018
Duke Scholars
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2018
Volume
123
Issue
2
Start / End Page
S79 / S80
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 1103 Clinical Sciences
Citation
APA
Chicago
ICMJE
MLA
NLM
Koeberl, D., Case, L., Smith, E. C., Li, Y., Walters, C., Hornik, C., … Kishnani, P. S. (2018). Correction of biochemical abnormalities and gene expression associated with improved muscle function in a phase I/II clinical trial of clenbuterol in Pompe disease patients stably treated with ERT. In Molecular Genetics and Metabolism (Vol. 123, pp. S79–S80). Elsevier BV. https://doi.org/10.1016/j.ymgme.2017.12.202
Koeberl, Dwight, Laura Case, Edward C. Smith, Yanzhen Li, Crista Walters, Christoph Hornik, Beth Thurberg, Deeksha Bali, Nenad Bursac, and Priya S. Kishnani. “Correction of biochemical abnormalities and gene expression associated with improved muscle function in a phase I/II clinical trial of clenbuterol in Pompe disease patients stably treated with ERT.” In Molecular Genetics and Metabolism, 123:S79–80. Elsevier BV, 2018. https://doi.org/10.1016/j.ymgme.2017.12.202.
Koeberl D, Case L, Smith EC, Li Y, Walters C, Hornik C, et al. Correction of biochemical abnormalities and gene expression associated with improved muscle function in a phase I/II clinical trial of clenbuterol in Pompe disease patients stably treated with ERT. In: Molecular Genetics and Metabolism. Elsevier BV; 2018. p. S79–80.
Koeberl, Dwight, et al. “Correction of biochemical abnormalities and gene expression associated with improved muscle function in a phase I/II clinical trial of clenbuterol in Pompe disease patients stably treated with ERT.” Molecular Genetics and Metabolism, vol. 123, no. 2, Elsevier BV, 2018, pp. S79–80. Crossref, doi:10.1016/j.ymgme.2017.12.202.
Koeberl D, Case L, Smith EC, Li Y, Walters C, Hornik C, Thurberg B, Bali D, Bursac N, Kishnani PS. Correction of biochemical abnormalities and gene expression associated with improved muscle function in a phase I/II clinical trial of clenbuterol in Pompe disease patients stably treated with ERT. Molecular Genetics and Metabolism. Elsevier BV; 2018. p. S79–S80.
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2018
Volume
123
Issue
2
Start / End Page
S79 / S80
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 1103 Clinical Sciences