Smith, E. C., Hopkins, S., Case, L. E., Childers, M. K., Han, S.-O., Spears, T. G., … Koeberl, D. D. (2022). Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Initial 104-Week Experience. In MOLECULAR THERAPY (Vol. 30, pp. 563–564).

Smith, Edward C., Sam Hopkins, Laura E. Case, Martin K. Childers, Sang-Oh Han, Tracy G. Spears, Christoph P. Hornik, Deeksha Bali, Priya S. Kishnani, and Dwight D. Koeberl. “Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Initial 104-Week Experience.” In MOLECULAR THERAPY, 30:563–64, 2022.

Smith EC, Hopkins S, Case LE, Childers MK, Han S-O, Spears TG, et al. Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Initial 104-Week Experience. In: MOLECULAR THERAPY. 2022. p. 563–4.

Smith, Edward C., et al. “Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Initial 104-Week Experience.” MOLECULAR THERAPY, vol. 30, no. 4, 2022, pp. 563–64.

Smith EC, Hopkins S, Case LE, Childers MK, Han S-O, Spears TG, Hornik CP, Bali D, Kishnani PS, Koeberl DD. Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Initial 104-Week Experience. MOLECULAR THERAPY. 2022. p. 563–564.